Human Genetic Disease and Gene Therapy
Lecture no. 33 from the course: Biochemistry and Molecular Biology: How Life Works
Taught by Professor Kevin Ahern | 29 min | Categories: The Great Courses Plus Online Science Course
Roughly 10,000 human diseases may be caused by mutations in single genes. Review the nature of genetic disorders, such as cystic fibrosis, hemophilia, and Alzheimer’s. Also examine diseases that emerge from mutations in mitochondrial DNA. Finally, assess the challenges of using gene therapy and other technologies to treat genetic diseases—issues that raise technical, legal, and ethical problems.